Skip to main content
Donate

Exciting News from UPenn

“This is a great decision by Dr. Wilson and that of The University of Pennsylvania to get the development of these gene therapies out of academia and into a well-resourced biotech environment that can execute more efficiently. This is exciting news for rare disease and for other companies that can now leverage the expertise of the 2nd company, Franklin, to help rapidly advance their bioanalytical and other contracted work. I’m thrilled!” – Dr. Allyson Berent, FAST Chief Science Officer

Read the full press release here.

The incredible academic work from The University of Pennsylvania is moving to biotech, where patients can be directly impacted. No one better to lead this effort than Dr. Jim Wilson.

The investigational gene therapy program for Angelman syndrome, known as GTP-220, is still owned by FAST and being run in collaboration with Dr. Wilson’s scientific team exactly as before. The change from an academic environment to a corporate entity will not impact the program deliverables or timelines. The money invested in the AS program is 100% being spent only on the GTP-220 program per the objectives of the sponsored research agreement, like every program we fund. Everyone is held to milestones and deliverables. FAST is continuing to closely control that program through IND and this news has no negative impact on the gene therapy program for Angelman syndrome. We expect this development will only improve efficiencies. This is good for all programs that were at UPenn, including AS.

More updates about investigational GTP-220 at the FAST Science Summit – registration is now open.

Disclaimer

This website contains information for a broad audience and may include information on current and upcoming programs that are not yet approved or accessible The information provided is for general informational purposes only and is not intended as medical advice, diagnosis, or treatment. While FAST strives to provide accurate and up-to-date information, the content on this site may not always reflect the most current research or clinical guidelines. The inclusion of clinical trial information, treatments or specific healthcare providers does not imply endorsement, recommendation or guarantee of safety, efficacy, or availability. Reliance on any information provided by this website is solely at your own risk. FAST disclaims any liability for any errors or omissions in the information provided or for any decisions made based on this information. For personalized medical advice or specific health concerns including participation in any clinical trial, please consult a qualified healthcare professional.