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Ultragenyx Community Update October 2024

The Phase 3 Efficacy and Safety Study of GTX-102 (ASO) in Pediatrics, sponsored by Ultragenyx, is now listed on ClinicalTrials.gov. Interested in learning more?

Watch the Ultragenyx Community Webinar

recording for more information.

Related

Ultragenyx Announces First Patient(s) Dosed in Pivotal Phase 3 Aspire Study Evaluating GTX-102 in Angelman Syndrome
Ionis Pharmaceuticals releases information on their planned phase 3 clinical trial for Angelman syndrome
Watch the ASF | FAST Ultragenyx Community Webinar recording
Neuren Pharmaceuticals announced top-line results from its Phase 2 clinical trial of NNZ-2591 in children with Angelman syndrome (AS). 

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