Non-viral delivery gene editing takes an important step forward for Angelman syndrome
A FAST-funded study unveils STEP-RNP, a non-viral gene editing platform showing improved motor, cognitive function in AS mice—an early but promising step toward treating Angelman syndrome.
Using Vocalization Testing to Improve Detection of Treatment Effects in Angelman Syndrome Models
New research adds ultrasonic vocalization testing to Angelman syndrome mouse studies, offering a more sensitive way to detect communication-related changes and evaluate future treatments.