Fundraise
Donate
Home/Industry/Foundation for Angelman Syndrome Therapeutics Announces Agreement with Apertura Gene Therapy for Access to Blood-Brain Barrier-Crossing Capsid

Foundation for Angelman Syndrome Therapeutics Announces Agreement with Apertura Gene Therapy for Access to Blood-Brain Barrier-Crossing Capsid

Read the press release

Related News

  • Industry

Oct 8, 2026: Ultragenyx Community Webinar

On October 8, 2026, ASF and FAST hosted a webinar with Ultragenyx after the announcement that their phase 3 trial for GTX-102 (aspire) did not meet primary or key secondary

  • Industry

MavriX Bio Announces FDA Rare Pediatric Disease Designation for Investigational MVX-220 for the Treatment of Angelman Syndrome

Read the press release

  • Research

Beyond UBE3A: New Conversations About Genotype, Variants, and Future Treatments

At INSYNC-AS 2026, researchers came together to examine how genes beyond UBE3A and differences within UBE3A itself may shape Angelman syndrome and future therapeutic development. Why can Angelman syndrome (AS)

  • Industry

Skylark Bio Expands Pipeline with First CNS Development Program, SKY-AS, Targeting UBE3A Restoration in Angelman Syndrome

Read press release

  • Industry

GTX-102 Phase 3 Results: What We Know, What We’re Still Learning, and Next Steps

FAST's CSO, Allyson Berent, addresses the Aspire trial results in a candid letter, exploring what the data mean, what questions remain, and how the community will move forward together.
  • Industry

Ultragenyx shares that GTX-102 trials will officially close on Oct 30, 2026.

Read the letter from Ultragenyx to the community: Angelman-Syndrome-Community-Update-9.16

View More News

What are you looking for?

Find information on Angelman syndrome, research, clinical trials, resources, and ways to get involved.